Investigators recently used a targeted drug to restore muscle strength and correct myotonia in mice with myotonic dystrophy. People with myotonic dystrophy experience progressive muscle weakness and ...
Oct 31 (Reuters) - Sarepta Therapeutics shares (SRPT.O), opens new tab fell nearly 44% on Tuesday, after its gene therapy for a progressive muscle-wasting disorder failed to meet the main goal in a ...
Cure Rare Disease (CRD) announced it has been awarded a $7.4 million grant from the California Institute for Regenerative Medicine (CIRM) to advance the development of a novel gene therapy for ...
In A Nutshell Brazilian researchers tested 72 panic disorder patients in a head-to-head trial: high-intensity sprint ...
BOSTON – People with myotonic dystrophy experience progressive muscle weakness and repeated episodes of painless muscle stiffness called myotonia. Investigators at Massachusetts General Hospital (MGH) ...